Engineering a broader bio-delivery system for gene therapy

The first gene therapies approved in the U.S. have undeniably transformed lives. Families describe the results with genuine wonder: Children who had been going blind can now see the moon for the first time, thanks to Spark Therapeutics’s Luxturna. Babies who would otherwise be paralyzed are crawling, rolling, and even learning to walk after treatment […]

Scaling up gene therapy to address global commercialization challenges

With clinical success, all eyes turn to gene therapy manufacturing and commercialization challenges Cell and gene therapies are here to stay as a new class of life-changing medicines. They recently headlined the fiscal year report issued by the FDA’s Center for Biologics Evaluation and Research (CBER), in which CBER Director Peter Marks prominently noted, “FY 2018 […]

Why reputation is more important than ever for biotech companies … and what you can do about it

“It takes twenty years to build a reputation, and five minutes to ruin it,” Warren Buffett said, and added “If you think about that, you’ll do things differently.” In biotech, a strong reputation is difficult to build, is even harder to establish quickly, and can be easily tarnished. So, what’s the landscape and what should […]