Patients and Families

ONE FOCUS: Striving to halt or reverse genetic disease

Patients drive us.

A deeper look

At AVROBIO, we work closely with patient communities to listen to and understand their views, experiences, and preferences.

We aspire to deliver therapies with the potential to significantly improve the lives of those affected by rare genetic disease.

We also understand that patient needs extend beyond just medicine. We collaborate with and support patient advocacy organizations to raise awareness, develop resources, and inform communities.

Learn more about our personalized approach to gene therapy.

We are focused first on developing one-dose treatments for lysosomal disorders.

Learn more about these genetic diseases.

Learn more about our
focus areas:


Explore more

Patient Advocacy

Connect with our patient advocacy and engagement team.

Our Pipeline

Learn more about our pipeline of investigational gene therapies.

Vector Space Blog

Dive into the latest science on gene therapy with our Vector Space Blog.