Can change your entire world?
At AVROBIO, we aim to halt or reverse disease with a single dose of gene therapy. Our goal is simple and powerful: We aim to enable individuals with genetic disease to live longer — free from disease progression, free from painful and debilitating symptoms and free from the burden of chronic treatment regimens.
OUR FOCUSA highly personalized therapy
Our investigational gene therapies start with the patient’s own stem cells. We are developing these treatments for several serious lysosomal disorders.
OUR APPROACHSolving the challenges of gene therapy
We've spent years developing a state-of-the-art platform to optimize gene therapies. We call it plato®.