ONE VISION, many insights
Our team works at the cutting edge of gene therapy.
We’re deeply involved in the global gene therapy community and take pride in sharing our knowledge, insights and discoveries.
Read pieces diving deep into the science of gene therapy.
These articles from our leadership team explore all aspects of the industry, from building a robust pipeline to preparing for commercial launch.
CloseToday is MPS Awareness Day (MPS II is also known as Hunter syndrome) and we want to recognize the incredible work that patient advocacy groups do year-round to support the Hunter syndrome community.
Learn more about Hunter syndrome and the patient advocacy groups’ efforts here: