A New Era of Medicine

Gene therapy represents a new paradigm in human health, with the potential to resolve unmet medical needs by addressing the underlying causes of disease.

Our Company

AVROBIO, Inc., a leader in lentiviral-based gene therapies, is a clinical stage company developing transformative, life-changing therapies that have the potential to transform patients’ lives in a single dose. The Company is focused on the development of its Phase 1 programs in Fabry disease and acute myeloid leukemia (AML), while actively building a pipeline of therapies to treat other rare diseases, and solid and liquid cancers.

Rare Disease Technology Overview

The Technology

Gene therapy has the potential to deliver dramatic disease modifying effects and potentially life-long cures from a single infusion of genetically-modified cells.