A New Era of Medicine
Gene therapy represents a new paradigm in human health, with the potential to resolve unmet medical needs by addressing the underlying causes of disease.
AVROBIO, Inc., a leader in lentiviral-based gene therapies, is a clinical stage company developing transformative, life-changing therapies that have the potential to transform patients’ lives in a single dose. The Company is focused on the development of its Phase 1 programs in Fabry disease and acute myeloid leukemia (AML), while actively building a pipeline of therapies to treat other rare diseases, and solid and liquid cancers.
Gene therapy has the potential to deliver dramatic disease modifying effects and potentially life-long cures from a single infusion of genetically-modified cells.