Patients and Families
ONE FOCUS: Striving to halt or reverse genetic disease
Patients drive us.
At AVROBIO, we work closely with patient communities to listen to and understand their views, experiences, and preferences.
We aspire to deliver therapies with the potential to significantly improve the lives of those affected by rare genetic disease.
We also understand that patient needs extend beyond just medicine. We collaborate with and support patient advocacy organizations to raise awareness, develop resources, and inform communities.
Learn more about our personalized approach to gene therapy.
We are focused first on developing one-dose treatments for lysosomal disorders.
Connect with our patient advocacy and engagement team.
Learn more about our pipeline of investigational gene therapies.
Vector Space Blog
Dive into the latest science on gene therapy with our Vector Space Blog.
Today is Rare Disease Day and we want to recognize the incredible work patient advocacy groups do year-round to raise awareness for the hundreds of millions of people around the world living with — and caring for — rare diseases.
Learn more: RAREDISEASEDAY.ORG | #RAREDISEASEDAY